The U.S. Food and Drug Administration approved Kebilidi (eladocagene exuparvovec-tneq), an adeno-associated virus ...

Kebilidi is the first approved gene therapy that can be directly administered to the brain. Its OK secures a priority review ...

PTC Therapeutics’ gene therapy, Kebilidi to treat AADC deficiency receives US FDA approval: Warren, New Jersey Friday, November 15, 2024, 10:00 Hrs [IST] PTC Therapeutics, Inc., ...

Sriansh Ojha was fully into his "terrible twos" on an April afternoon at Cincinnati Children's as he squealed and chased his ...

Significant changes are coming to ABL Space Systems. The leader of the seven year old startup took to social media last night ...

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A review of things you need to know before you sign off on Thursday; REINZ data mixed, inflation pressures ease, Kookmin to quit NZ, Rennie gets top Treasury job, Bank of China here 10 years, swaps ...