An investigational gene therapy for a rare neurodegenerative disease that begins in early childhood, known as giant axonal neuropathy (GAN), was well tolerated and showed signs of therapeutic ...

Giant axonal neuropathy (GAN) is a rare, genetic neurodegenerative disorder in which large nerve fibers in the brain (axons) ...

Bamboo has pre-clinical treatments for Duchenne muscular dystrophy, Friedreich’s Ataxia and Canavan disease, and a phase 1 asset for Giant Axonal Neuropathy. Unlike Biogen and its investment of ...